Agenda at a GlanceNote: titles and times subject to change |
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Day 1 Evening Session Wednesday, October 29, 2025 |
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| Introduction & Greetings from PRF Medical Director Leslie Gordon, MD, PhD, Executive Director Audrey Gordon, Esq., Board Chair Scott Berns, MD, MPH, FAAP |
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| Merlin Waldron (moderator), Megan Nighbor, Griffin Ray, Ricardo Zanolli, Nathan Falcone, Michiel Vandeweert | “Coming of Age” Conversations: Young adults with HGPS as Research Partners | |
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Musical Kick-off with Francis Collins, MD, PhD National Human Genome Research Institute, National Institutes of Health, Bethesda, MD |
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DINNER and Networking Evening |
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Day 2 Morning Session Thursday, October 30, 2025 |
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Current Treatment Trial Outcomes in Progeria Moderator: Mark Kieran, MD, PhD, Day One Bio. |
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| লেসলি গর্ডন, এমডি, পিএইচডি Brown University, Hasbro Children’s Hospital, Boston |
Long-term Natural History Lonafarnib Treatment Trial | |
| মনিকা ক্লেইনম্যান, এমডি Boston Children’s Hospital, Boston, MA |
Phase 2a Progerinin Clinical Treatment Trial for Progeria | |
| Barbara Natke, PhD Progeria Research Foundation, Peabody, MA |
Tools for Pivotal Science and Medicine in Progeria: Antibody and Biomarker Assay Development |
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| Sunil Ghelani, MD Progeria Research Foundation, Peabody, MA |
First-ever Aortic and Coronary Artery Calcium Computed Tomography Clinical Trial Study in Progeria | |
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LUNCH, Informal Poster Viewings and Networking |
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Day 2 Afternoon Session Thursday, October 30, 2025 |
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Cardiovascular Disease in HGPS and Aging Moderator: Maria Eriksson, PhD |
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| মারিয়া এরিকসন, পিএইচডি Karolinska Institute, Sweden |
Single-cell analysis reveals the phenotypic landscape of arterial cells in Progeria | |
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Shannon Lyon, MD Keri Shafer, MD Sheila Hegde, MD |
New discoveries in Cardiac Measures of Disease in Progeria and Aging through Echocardiography | |
| Kan Cao, PhD Univ. of Maryland, College Park, MD |
Angiopoietin-2 reverses endothelial cell dysfunction in Progeria vasculature | |
| Ricardo Villa Bellosta, PhD CiMUS and USC, Av. Barcelona, Spain |
Progeria and Vascular Calcification: Diet and Treatments | |
| LATE-BREAKING DATA PRESENTATION | To Be Determined – Cutting Edge Discoveries | |
| 7th INNING STRETCH and Networking Time | ||
| লাইটনিং পোস্টার সেশন | 1 মিনিট এবং 1 স্লাইড প্রতি পোস্টার উপস্থাপক | |
| DINNER and Informal Conversation | ||
Day 2 Evening Poster Session Thursday, October 30, 2025 |
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7:00-8:00 Even-Numbered Posters Formally Presented 8:00-9:00 Odd-Numbered Posters Formally Presented |
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Day 3 Sunrise Session: Coffee Talk with Patients and Families Friday, October 31, 2025 |
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Day 3 Morning Session Friday, October 31, 2025 |
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Progeria Treatment Discovery for a Healthy Future Moderator: Francis Collins, MD, PhD |
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| David Liu, PhD, Broad Institute, MIT, Cambridge, MA & ফ্রান্সিস কলিন্স, এমডি, পিএইচডি |
ProSPER: PROgeria Streamlined Platform gene Editing for Rare diseases | |
| Nizar Saad, PhD Nationwide Children’s Hospital, Columbus, OH |
Development of a miRNA-based Gene Therapy for Hutchinson-Gilford Progeria Syndrome (HGPS) | |
| Ning Shen, PhD, Professor Zhejiang Univ. Medical School, Hangzhou, China |
AI-driven therapeutic antisense oligonucleotide for Hutchinson-Gilford Progeria | |
| Silvia Ortega Gutierrez, PhD Complutense University, Madrid Spain |
Reduction of progerin levels by small molecules as a new approach for treating Progeria | |
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LUNCH and Networking |
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Day 3 Afternoon Session Friday, October 31, 2025 |
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Endocrine and GI Disease in Progeria Moderator: Vicente Andres, PhD |
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| ভিসেন্ট আন্দ্রেস, পিএইচডি Spanish National CV Res. Center, Madrid, Spain |
Lipodystrophy in Progeria and Aging | |
| Laurence Arbibe, PhD INSERM Institut Necker Enfants Malades, Paris, Fr. |
Unraveling accelerated intestinal ageing in HGPS physiopathology: an integrative approach | |
| Susana Gonzalo, PhD St. Louis University, St Louis, MO |
Cathepsin-L mediated remodeling of the nuclear proteome | |
| LATE BREAKING DATA PRESENTATION | To Be Determined – Cutting Edge Discoveries | |
| Poster Elevation Talk by Junior Investigator | To Be Determined after Poster Abstract Submissions | |
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NETWORKING TIME |
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Workshop Wrap-up:
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Moderators: Francis Collins, Mark Kieran, Leslie Gordon |
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